Found 4 Pompe Disease trials
A listing of Pompe Disease medical research trials actively recruiting patient volunteers. Search for closest city to find more detailed information on a research study in your area.
A STUDY TO ASSESS THE LONG-TERM SAFETY AND EFFICACY OF INTRAVENOUS ATB200 CO-ADMINISTERED WITH ORAL AT2221 IN ADULT SUBJECTS WITH LATE-ONSET POMPE DISEASE
Phase 3
A STUDY TO ASSESS THE LONG-TERM SAFETY AND EFFICACY OF INTRAVENOUS ATB200 CO-ADMINISTERED WITH ORAL AT2221 IN ADULT SUBJECTS WITH LATE-ONSET POMPE DISEASE
HONU
The primary objective of this observational study is to assess iAMD disease progression, by the timeline and rates of conversion for high-risk iAMD at baseline to more advanced dry AMD stages, such as nascent geographic atrophy (nGA) or incomplete retinal pigment epithelium and outer retinal atrophy (iRORA), and subsequently from …
Aqueous Humor Proteomics
PURPOSE The goal of this study is to measure the levels of over 11,000 proteins in the aqueous humor and correlate it with single-cell transcriptomics data. This will improve understanding of the molecular mechanisms and cell types contributing to dry AMD, POAG, and Stargardts disease. This will allow us to …
