-
A Phase 1b Multicenter Open-Label Safety Tolerability and Activity Study of SYNT001 in Subjects with Chronic Stable Warm Autoimmune Hemolytic ...
WAIHA is caused by antibodies (proteins) that attach to red blood cells and causes their destruction. This causes anemia, which ...
Exact
Phase 
-
ALN-AT3SC-003: ATLAS INH: A Phase 3 Study to Evaluate the Efficacy and Safety of Fitusiran in Patients with Hemophilia A ...
This study will evaluate the efficacy and safety of fitusiran compared to on-demand treatment with bypassing agents, as determined by ...
Exact
Phase 
-
Clinical research study to assess ability of eltrombopag to induce sustained remission in subjects with Immune Thrombocytopenia who are refractory ...
This research study is to find out if the study drug eltrombopag also known as Revolade/Promacta can help those ...
Exact
Phase 
-
Phase 3 open label single arm study to evaluate efficacy and safety of FIX gene transfer with PF-06838435 (rAAV Spark100-hFIX-Padua ...
The research study is being conducted to test the safety and effectiveness of the study drug which is a gene ...
Exact
Phase
Showing - of trials